Rare Toolbox

+70 policy recommendations informed by peer-reviewed evidence, best practices & real-world learnings from around the world, and endorsed by APEC Health Ministers

White paper developed through multistakeholder consultations in Chile, Peru, and Malaysia, analyzing how the COVID-19 pandemic impacted rare disease policymaking

Describes the "co-benefits" of RD policy, planning & programs: how they strengthen health systems, enhance research & innovation, and improve outcomes for prevalent conditions

Evidence-informed policy paper outlining global and APEC-focused reforms to streamline regulatory review and approval of rare disease therapies, including 6 priority action areas.

Practical design tool for national rare disease policies and plans, offering an orientation typology, 9 design components with trade-offs, a staged maturity pathway, and a self-diagnostic, aligned with the APEC Action Plan's 10 pillars.

Supplement to the APEC Action Plan on Rare Diseases with rare disease policy recommendations organized by the ministry or government entity responsible for implementation

Policy brief developed through multistakeholder consultation in Thailand, recommending approaches to accelerate implementation of the APEC Action Plan on Rare Diseases

Peer-reviewed summary of evidence, policies & challenges for enhancing access to rare disease diagnosis & treatment from a group of experts including several GRDPN members

Evidence-informed policy paper outlining global and APEC-focused reforms to improve HTA for rare disease therapies, including 11 recommended policy directions.