Rare Toolbox
Create tools to help governments & partners make political & policy decisions for rare diseases: case studies, white papers, policy briefs, guidelines, checklists & frameworks
COVID-19: Lessons for Rare Disease Policy & Resilient Health Systems
White paper developed through multistakeholder consultations in Chile, Peru, and Malaysia, analyzing how the COVID-19 pandemic impacted rare disease policymaking
Co-Benefits of Rare Disease Policy, Planning, and Programs
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Optimizing Regulatory Review & Approval for Orphan Drugs
Coming soon
A Typology of National Rare Disease Plans & Policies
Coming soon
Interagency Checklist
Supplement to the APEC Action Plan on Rare Diseases with rare disease policy recommendations organized by the ministry or government entity responsible for implementation
Case Study: Opportunities for Rare Disease Policy in Thailand
Policy brief developed through multistakeholder consultation in Thailand, recommending approaches to accelerate implementation of the APEC Action Plan on Rare Diseases
Optimizing HTA & Reimbursement Policy for Orphan Drugs
Coming soon
RD-GPT: An AI Assistant for Rare Disease Policymaking & Planning
Coming soon
What Policymakers & Partners Say
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Hon. Khairy Jamaluddin, Former Minister of Health, Malaysia
"This is a three-corner collaboration between Ministry representatives, universities, and pharmaceutical companies that together set up the APEC Action Plan on Rare Diseases for use as a guide in providing the best services for this group of patients." (CodeBlue, 2021)